APCCC 2024: How to Manage Side Effects of PARP Inhibitors?

(UroToday.com) The 2024 Advanced Prostate Cancer Consensus Conference (APCCC) meeting featured a session on the management of metastatic CRPC (mCRPC), and a presentation by Dr. Elena Castro discussing how to manage side effects of PARP inhibitors. Dr. Castro notes that in the PARP inhibitor monotherapy trials, there were frequent adverse events:


Comparatively, there were also frequent adverse events in the ARPI + PARP inhibitor combination trials, although there were no differences in toxicity by HRR status:

Of note, frequent side effects tend to occur early in the treatment course. When looking at the three PARP inhibitor + ARPI combination trials (MAGNITUDE,1 PROpel,2 and TALAPRO-2),3 Dr. Castro highlighted that there are several adverse events of special interest. Anemia is arguably the most common adverse event grade >= 3, ranging from 16% in the PROpel trial to 46% in the TALAPRO-2 trial. Hypertension was also notable in the MAGNITUDE trial at 15% grade >= 3. Moreover, it appeared that venous thromboembolism was frequent, including 4.7% of patients in MAGNITUDE with a pulmonary embolism, 7% in PROpel, and 3% in TALAPRO-2. A side-by-side comparison of the three trials comparing adverse events is as follows:three PARP inhibitor + ARPI combination trials (MAGNITUDE,1 PROpel,2 and TALAPRO-2)
Knowing how to manage hematological side effects from PARP inhibitors is important and is based on the grade of adverse event. Patients with grade 1 anemia (hemoglobin >= 10 g/dL) are monitored, whereas those with grade 2 anemia (hemoglobin <10 - >= 8 g/dL) should have a dose interruption, transfusions till the hemoglobin reaches 9 g/dL, and frequent monitoring. No dose reduction is required when the patient is started back on therapy. Grade 3-4 anemia (hemoglobin < 8 g/dL) is managed similarly to grade 2 anemia, but the dose is reduced when restarted. The following treatment algorithm also highlights the management for subsequent occurrences:
PARP inhibitor treatment algorithm also highlights the management for subsequent occurences
The management of neutropenia, leukopenia, and thrombocytopenia is as follows:
management of neutropenia, leukopenia, and thrombocytopenia
Dr. Castro also mentioned management options for non-hematologic side effects:

  • Nausea/vomiting: prokinetics and 5-HT3 receptor antagonists, anti-emetics, light meals with an anti-emetic before treatment, and avoidance of a CYP3A4 inhibitor with olaparib
  • Diarrhea/constipation: loperamide or laxatives
  • Fatigue: non-pharmacologic treatments (physical activity), psychostimulants for more symptomatic patients
  • Hypertension: antihypertensives
  • Renal toxicity: an increase in creatinine may not reflect a true decline in GFR (ie. rucaparib can inhibit the renal transporters MATE1 and MATE2)

Generally, the non-hematological adverse events are handled as follows, also based on the grade of severity:
non-hematological adverse events are handled as follows, also based on grade of severity
Myelodysplastic syndromes are clonal hematopoietic neoplasms characterized by the combination of persistent unexplained cytopenias and morphologic dysplasias, and a propensity to progress to bone marrow failure or acute myeloid leukemia. Acute myeloid leukemia is a clonal expansion of immature “blast cells” in the peripheral blood and bone marrow resulting in ineffective erythropoiesis and bone marrow failure (cytopenias). Risk factors for developing these entities include age > 60 years, genetic predisposition, chemotherapy, and environmental exposure. With regards to PARP inhibitor treatment and development of these conditions, Dr. Castro recommends the following:PARP inhibitor treatment and development of hematological conditions
Dr. Castro then discussed a recent meta-analysis assessing myelodysplastic syndrome and acute myeloid leukemia in patients treated with PARP inhibitors.4 Among 18 randomized clinical trials (n = 7,307 patients), PARP inhibitors significantly increased the risk of myelodysplastic syndrome and acute myeloid leukemia compared with placebo treatment (OR 2.63, 95% CI 1.13-6.14, p = 0.026). The incidence of myelodysplastic syndrome and acute myeloid leukemia across PARP inhibitor groups was 0.73% (95% CI 0.50-1.07; 21 events out of 4,533 patients) and across placebo groups was 0.47% (0.26-0.85; three events out of 2,774 patients). 

In this same publication,4 a review of the WHO VigiBase database (cut off May 3, 2020) was undertaken, with a reported 178 cases of myelodysplastic syndrome (n = 99) and acute myeloid leukemia (n = 79) related to PARP inhibitors,4 including 7 for patients with breast cancer, 119 for ovarian cancer, 3 for pancreatic cancer, 10 for prostate cancer, and 1 for vulvar cancer. The median age at diagnosis was 64 years (range: 38-81), the median PARP inhibitor duration was 9.8 months (range: 3.6 – 17.4), and the latency period from first PARP inhibitor exposure to myelodysplastic syndrome was 17.8 months, and was 20.6 months for acute myeloid leukemia. Dr. Castro notes that this is a shorter latency period than with conventional chemotherapy, which is typically 3-5 years.

Dr. Castro concluded her presentation discussing how to manage side effects of PARP inhibitors with the following take-home messages:

  • In BRCA/HRR patients, PARP inhibitor benefits largely outweigh the risks associated with potential adverse events
  • Most toxicities are acute and can be safely managed, however, regular monitoring is needed (particularly in the first 3-4 months)
  • Myelodysplastic syndrome and acute myeloid leukemia are delayed side effects
    • They are infrequent, although the true incidence may be underestimated
    • Should be suspected in the event of persistent/recurrent cytopenias
    • Should be considered for future trials/treatment strategies

Presented by: Elena Castro, MD, PhD, Medical Oncologist, Hospital Universitario 12 de Octubre, Madrid, Spain

Written by: Zachary Klaassen, MD, MSc - Urologic Oncologist, Associate Professor of Urology, Georgia Cancer Center, Wellstar MCG Health, @zklaassen_md on Twitter during the 2024 Advanced Prostate Cancer Consensus Conference (APCCC) Meeting, Lugano, Switzerland, Thurs, Apr 25 - Sat, Apr 27, 2024. 

References:

  1. Chi KN, Rathkopf D, Smith MR, et al. Niraparib and abiraterone acetate for metastatic castration-resistant prostate cancer. J Clin Oncol. 2023 Jun 20;41(18):3339-3351.
  2. Saad F, Clarke NW, Oya M, et al. Olaparib plus abiraterone versus placebo plus abiraterone in metastatic castration-resistant prostate cancer (PROpel): final prespecified overall survival results of a randomized, double-blind, phase 3 trial. Lancet Oncol. 2023 Oct;24(10):1094-1108.
  3. Agarwal N, Azad AA, Carles J, et al. Talazoparib plus enzalutamide in men with first-line metastatic castration-resistant prostate cancer (TALAPRO-2): A randomized, placebo-controlled, phase 3 trial. Lancet. 2023 Jul 22;402(10398):291-303.
  4. Morice PM, Leary A, Dolladille, et al. Myelodysplastic syndrome and acute myeloid leukemia in patients treated with PARP inhibitors: A safety meta-analysis of randomized controlled trials and a retrospective study of the WHO pharmacovigilance database. Lancet Haematol. 2021 Feb;8(2):e122-e134.

Related Content:

Gillessen, S. et al. (2024) ‘Management of patients with advanced prostate cancer. report from the 2024 Advanced prostate cancer consensus conference (APCCC)’, European Urology [Preprint]. doi:10.1016/j.eururo.2024.09.017.